Differences

This shows you the differences between two versions of the page.

Link to this comparison view

Both sides previous revision Previous revision
Next revision
Previous revision
ngly1_deficiency [2025/03/11 02:26] Scott Larsonngly1_deficiency [2025/04/18 20:40] (current) – external edit 127.0.0.1
Line 22: Line 22:
   * Nystagmus- rare   * Nystagmus- rare
 ====Other Findings==== ====Other Findings====
-  * increased liver transaminases +  * Increased liver transaminases 
-  * polyneuropathy+  * Polyneuropathy
 ====Etiology==== ====Etiology====
   * Autosomal Recessive   * Autosomal Recessive
-  * loss-of-function variants of the NGLY1 encoding N-glycanase 1+  * Loss-of-function variants of the NGLY1 encoding N-glycanase 1
     * an enzyme that removes the sugar moiety from proteins     * an enzyme that removes the sugar moiety from proteins
     * cleaves N-glycans to generate deglycosylated proteins and oligosaccharides containing 1-amino-GlcNac     * cleaves N-glycans to generate deglycosylated proteins and oligosaccharides containing 1-amino-GlcNac
     * degrades misfolded proteins in the endoplasmic reticulum      * degrades misfolded proteins in the endoplasmic reticulum 
 ====Resources==== ====Resources====
-  * [[link|Title]]+  * {{ ::ocular_feature_of_ngly1_deficiency_from_a_prospective_lingitudinal_cohort_2023.pdf |Frater CH et al. Ocular features of NGLY1 deficiency from a prospective longitudinal cohort. J AAPOS 2024;28:103925}}
  
 {{tag>syndrome}} {{tag>syndrome}}